@misc{indiciae38afa31a2cb6, title = {Rescue of a panel of Hemophilia A-causing 5'ss splicing mutations by unique Exon-specific U1snRNA variants.}, author = {Laura Peretto and Claudia D'angiolillo and Paolo Ferraresi and Dario Balestra and Mirko Pinotti}, year = {2025}, doi = {10.1186/s10020-025-01176-8}, url = {https://pubmed.ncbi.nlm.nih.gov/40148820/}, note = {Source identifier: 40148820} }