TY  - RPRT
TI  - Rescue of a panel of Hemophilia A-causing 5'ss splicing mutations by unique Exon-specific U1snRNA variants.
AU  - Laura Peretto
AU  - Claudia D'angiolillo
AU  - Paolo Ferraresi
AU  - Dario Balestra
AU  - Mirko Pinotti
PY  - 2025
DO  - 10.1186/s10020-025-01176-8
UR  - https://pubmed.ncbi.nlm.nih.gov/40148820/
ID  - 40148820
ER  -