@misc{indiciae865cf5709ac9, title = {Treatment of a severe vascular disease using a bespoke CRISPR-Cas9 base editor in mice.}, author = {Christiano R R Alves and Sabyasachi Das and Vijai Krishnan and Leillani L Ha and Lauren R Fox and Hannah E Stutzman and Claire E Shamber and Pazhanichamy Kalailingam and Siobhan McCarthy and Christian L Lino Cardenas and Claire E Fong and Takahiko Imai and Sunayana Mitra and Shuqi Yun and Rachael K Wood and Friederike M C Benning and Kangsan Roh and Joseph Lawton and Nahye Kim and Rachel A Silverstein and Joana Ferreira da Silva and Demitri de la Cruz and Rashmi Richa and Jun Xie and Heather L Gray-Edwards and Rajeev Malhotra and David Y Chung and Luke H Chao and Shengdar Q Tsai and Casey A Maguire and Mark E Lindsay and Benjamin P Kleinstiver and Patricia L Musolino}, year = {2025}, doi = {10.1038/s41551-025-01499-1}, url = {https://pubmed.ncbi.nlm.nih.gov/40935887/}, note = {Source identifier: 40935887} }