@misc{indiciae6a60d91adc00, title = {Exa-cel in Children with Transfusion-Dependent \&\#x3b2;-Thalassemia or Sickle Cell Disease.}, author = {Haydar Frangoul and Josu de la Fuente and Yogi Chopra and Roland Meisel and Persis J Amrolia and Mattia Algeri and Akshay Sharma and Maria Domenica Cappellini and Selim Corbacioglu and Antonis Kattamis and Stephan Lobitz and Mariane de Montalembert and Damiano Rondelli and Sujit Sheth and Martin H Steinberg and Mark C Walters and Kevin Boerner and Tina Liu and Sakellarios Zairis and William Hobbs and Stephan A Grupp and Franco Locatelli and CLIMB THAL-141 and CLIMB SCD-151 Study Groups}, year = {2026}, doi = {10.1056/nejmoa2603387}, url = {https://pubmed.ncbi.nlm.nih.gov/42274009/}, note = {Source identifier: 42274009} }