Duchenne muscular dystrophy.

J R Gorospe; E P Hoffman

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PubMed · 1457273

Duchenne muscular dystrophy.

J R Gorospe·E P Hoffman

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Abstract

Advances in the understanding of the genetic basis for Duchenne muscular dystrophy over the past 4 years has led to the quick application of molecular diagnostics. More recently, attention has turned towards acquiring a better understanding of dystrophin biochemistry and the pathophysiologic consequences of dystrophin deficiency.

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Dystrophin Genetic Therapy Humans Models, Biological Muscular Dystrophies Journal Article Review

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J R Gorospe, E P Hoffman. 1992. Duchenne muscular dystrophy.. https://pubmed.ncbi.nlm.nih.gov/1457273/

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