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Pharmaceutical prospects for RNA interference.

Raymond M Schiffelers·Martin C Woodle·Puthupparampil Scaria
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Abstract

RNA interference has proven to be a powerful tool in gene function validation. Recently, the first studies were published reporting a disease-modulating activity of the technique, suggesting a promise for RNA interference as a novel therapeutic strategy. This review discusses the recent advancements in realizing the clinical utility of RNA-interference.

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AnimalsDrug Delivery SystemsHumansRNA InterferenceRNA, Small InterferingTechnology, PharmaceuticalJournal ArticleResearch Support, Non-U.S. Gov'tReview

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Raymond M Schiffelers, Martin C Woodle, Puthupparampil Scaria. 2004. Pharmaceutical prospects for RNA interference.. https://doi.org/10.1023/b%3Apham.0000012145.49054.6c

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