alpha-glucosidase (CHO) (Genzyme).

Robin H Lachmann

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PubMed · 15535432

alpha-glucosidase (CHO) (Genzyme).

Robin H Lachmann

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Abstract

Genzyme General is developing recombinant human alpha-glucosidase, produced in mammalian cell culture, as a potential treatment for Pompe disease. By July 2004, enrollment was completed in two clinical trials and an observational study in adults. Genzyme was planning to file for regulatory approval in Europe during 2004, followed by filings in the US and Japan in mid-2005.

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Animals Clinical Trials as Topic Glycogen Storage Disease Type II Humans Recombinant Proteins Structure-Activity Relationship Treatment Outcome alpha-Glucosidases Journal Article Review

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Robin H Lachmann. 2004. alpha-glucosidase (CHO) (Genzyme).. https://pubmed.ncbi.nlm.nih.gov/15535432/

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