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PubMed · 1629146

Gene therapy: a status report.

S Agarwal·R Khardori·N Khardori
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Abstract

Gene therapy is a way to treat disease by transfer of genetic material into the cells of a diseased organism. Generally it is transferred in the form of one or few genes. There is a tremendous potential for application of this technique to the treatment of human hereditary diseases, particularly single gene disorders. Due to ethical and practical reasons, it is currently being used only as somatic cell therapy but it could be achieved by germline also. The major problem in gene therapy is achieving an efficient gene transfer and a persistent gene expression in appropriate somatic cells.

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AnimalsCloning, MolecularEthics, MedicalGenetic Diseases, InbornGenetic EngineeringGenetic TherapyHumansMicePromoter Regions, GeneticResearchTransfectionJournal ArticleReview

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S Agarwal, R Khardori, N Khardori. 1992. Gene therapy: a status report.. https://pubmed.ncbi.nlm.nih.gov/1629146/

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